From data lakes to streamlined production, Kriya, Opus, and Epicrispr discuss how technology is improving their operations.
StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models. Gene therapy can effectively treat various ...
Pharmaceutical Technology on MSN
UniQure to seek approval of Huntington’s gene therapy after FDA U-turn
uniQure confirmed it will submit its BLA in Q3 2026, though there is still a required confirmatory study to conduct.
From early research to quality control, maintaining analytical continuity is no easy task. Could a single sequencing workflow help simplify analytical assessment?
The period between the 1920s and 1950s was a time of significant progress and exciting discoveries in gene therapy history and biomedicine. Groundbreaking advances in understanding inherited DNA and ...
U.S. market projected to reach USD 13.18 Billion and Europe USD 13.96 Billion by 2035 as cell and gene therapy outsourcing ...
Casgevy sickle cell gene therapy is now FDA-approved for children as young as two, opening access for 5,500 more U.S. kids.
State-of-the-art gene therapy provides new treatment option for children 2 years and older with life-threatening blood disorder ...
Black Information Network on MSN
23-year-old cured of sickle cell after two-year gene therapy journey
Daniel Cressy became the first person in Louisiana — and the Gulf South — to be functionally cured of sickle cell disease ...
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