2 days ago · Read all about gene therapy including current medical research on switching therapeutic genes on and off, light-activated gene therapy and gene silencing.

5 days ago · Rapid scientific advances have put the gene therapy field at the forefront of biomedical research. But, as recent setbacks have shown, researchers and drugmakers still face major challenges.

Mar 5, 2026 · Speaking on a call with reporters Thursday, the senior FDA official defended the agency’s demand that uniQure conduct another sham-controlled trial for its Huntington’s gene therapy and ...

Stay current on the latest breakthroughs and news in the cell and gene therapy field. Explore our newsroom for press releases, society announcements, and stories on the science driving our …

Feb 9, 2026 · Find all the latest on gene therapy at Medical Xpress. Your go-to source for news, research, and medical breakthroughs.

Nov 13, 2025 · Today, as Chief Science Officer at the Foundation for Angelman Syndrome Therapeutics (FAST), she’s turning that urgency into progress, advancing the first gene therapy programs for …

4 days ago · Find the latest research papers and news in Gene Therapy. Read stories and opinions from top researchers in our research community.

Stay up to date on the latest news and advances in gene editing, including CAR-T cell therapy, stem cell research, and the allure of regenerative medicine.

Oct 23, 2025 · Patients have experienced life-changing improvements in their vision thanks to a new gene therapy developed… Gene therapy is a medical technique that involves modifying the genes …

Mar 2, 2026 · Days after FDA Commissioner Marty Makary appeared to malign uniQure’s AMT-130 in an interview with CNBC, the agency confirmed to the biotech that a sham surgery–controlled study is …